07/10/2016
Sanfilippo Syndrome is often diagnosed when parents realize their child is missing development milestones, around the ages 2 to 6 years. Due to the rarity of the disease, it can take years to receive a proper diagnosis. As Sanfilippo progresses, children will typically develop increasingly severe activity and behavioral problems. Gradually, they lose all of the skills and abilities they had once learned, such as walking, eating, and speaking.
Together we can make hope happen! In the past 2 years, new Sanfilippo clinical trials and gene therapy treatments have become a reality through our private grassroots fundraising efforts - but more support is needed! Proceeds from A Night of Hope & WILL Power, will help more children receive the medical treatments that are their only chance at life. Visit our donations page to learn how you can help turn hope into happen: https://hopetohappen.com